Tag: SMA

Biogen scoops sixth Prix Galien award with UK for life-changing rare...

Biogen was announced as the winner of the Orphan Product Award at last night’s UK Prix Galien 2018, for Spinraza, which in 2017 became...
NURTURE

New data show Spinraza beneficial in the treatment of spinal muscular...

Rates of survival are higher, and respiratory intervention rates are lower, in 25 infants with presymptomatic 5q spinal muscular atrophy (SMA) treated with Spinraza...

Preliminary study suggests drug may help infants with Spinal Muscular Atrophy

A preliminary study suggests that an investigational drug may help increase protein levels in infants with spinal muscular atrophy. The results of the open label study were...