Tag: Evrysdi
Significant improvements in survival and developmental milestones for Type 1 SMA...
Symptomatic Type 1 spinal muscular atrophy (SMA) infants treated with Evrysdi (risdiplam) showed significant improvements in survival, motor milestones, and motor function compared to...
Evrysdi approved in Japan for the treatment of spinal muscular atrophy
PTC Therapeutics has announced that Evrysdi (risdiplam) has been approved in Japan by the Japanese Ministry of Health, Labor and Welfare for the treatment of spinal...